HEMOPHILIA AND NON-CANCER DISORDERS
23.0606: A Long-Term Follow-Up Study in Subjects with Severe Hemophilia A Who Received BMN 270, an Adeno-Associated Virus Vector Mediated Gene Transfer of Human Factor VIII in a Prior BioMarin Clinical Trial
Principal Investigator: Vivek Sharma, MD, FACP
Phase: Choose an item.
Description: The BMN 270 clinical development program consists of multiple interventional studies designed to assess the safety and efficacy of a single infusion of BMN 270 for at least 5 years post-infusion. This long-term follow-up study is needed to help further understand the long-term safety of BMN 270 beyond 5 years and to assess the durability of efficacy.
ClinicalTrials.gov: https://clinicaltrials.gov/study/NCT05768386?term=NCT05768386&rank=1
08.0388 - Protocol for the Cancer Database and Specimen Repository (CDSR) at the Brown Cancer Center (Previous Lung Repository).
Principal Investigator: Rebecca Redman, M.D.
Description: The mission of the Cancer Database and Specimen Repository (CDSR) is to collect clinical information and samples of human specimens from cancer patients and from control patients for research, and to distribute specimens to researchers for the advancement of science.