Treatment of Other Diseases
Active at Duke University
There are a variety of diseases and disorders that are referred to as inherited abnormalities of bone marrow derived cells. This can be a red blood cell disorder, other immunodeficiency disorder, or genetic error of metabolism, which is a result of some abnormality in the blood cells.
These disorders include but are not limited to:
- Red blood cell disorders such as Thalessemia
- Other immunodeficiency disorders
- Inherited metabolic enzyme disorders
Principal Investigator - Joanne Kurtzberg, M.D